Phenylketonuria (PKU) R&D Pipeline Analysis Report, Q4 2020
Phenylketonuria (PKU) Pipeline Overview
The Q4 Phenylketonuria (PKU) pipeline report is part of the VPA Metabolic Disorder disease pipeline service. This quarterly review describes the pipeline of drugs under development for Phenylketonuria (PKU), provides an update on the mechanism of action and targets, licensing and collaboration opportunities, company profiles including their business information, and market developments.
Phenylketonuria (PKU) Disease Types, Symptoms, Causes, and Available Treatment Options
The comprehensive report on the indication presents Phenylketonuria (PKU) disease overview, Phenylketonuria (PKU) types, Phenylketonuria (PKU) symptoms, causes, and FDA/EMA approved treatment options.
Phenylketonuria (PKU) Pipeline Trends and Insights
The year 2020 witnessed progress in innovations and the number of pipeline agents researched for Phenylketonuria (PKU) indication. The report presents near-term and long-term pipeline development trends and potential insights.
Phenylketonuria (PKU) Company Trends and Insights
The report analyzes the development progress, current status, investments, partnerships, and other developments of 15 companies. Business profiles and contact details of the companies actively perusing Phenylketonuria (PKU) pipeline are assessed.
Phenylketonuria (PKU) R&D Pipeline Development Phase Trends and Insights
From the discovery stage of development to phase 3 development, all the potential pipeline drug candidates are analyzed in the report. Phenylketonuria (PKU) discovery stage, research stage, Phase 1, phase 2, Phase 3, IND enabling studies are provided in the research.
Small Phenylketonuria (PKU) companies look for licensing and collaboration partners
High R&D costs and long duration pose challenges for small companies operating in the industry. Further, the presence of large companies and stringent regulations act as barriers for Phenylketonuria (PKU) pipeline development companies. Accordingly, a significant portion of small companies presents potential licensing and collaboration opportunities.
Phenylketonuria (PKU) Pipeline Market News and Developments during 2020
The Phenylketonuria (PKU) industry news, pipeline research, market developments including advancement in phases, pre-clinical study results, clinical trial launches, acquisitions and mergers, regulatory approvals, and others are included in the report.
Phenylketonuria (PKU) Mechanism of Action and Targets
Leading Mechanism of Action and targets being researched by all the companies and their progress is included. New mechanisms of actions introduced during the year, route of administration, orphan drug designation, and others are provided in the study.
New molecular entity details
Drug candidates identified as new molecular entities by FDA, EMA, and other regulators are included in the research.
Sources and Research Methodology
Data is updated daily across diseases in the infectious pipeline service. We review our quarterly pipeline reports for the latest 5 years to present longitudinal insights.
Scope and Coverage
The Q4 Phenylketonuria (PKU) pipeline report is part of the VPA Metabolic Disorder disease pipeline service. This quarterly review describes the pipeline of drugs under development for Phenylketonuria (PKU), provides an update on the mechanism of action and targets, licensing and collaboration opportunities, company profiles including their business information, and market developments.
Phenylketonuria (PKU) Disease Types, Symptoms, Causes, and Available Treatment Options
The comprehensive report on the indication presents Phenylketonuria (PKU) disease overview, Phenylketonuria (PKU) types, Phenylketonuria (PKU) symptoms, causes, and FDA/EMA approved treatment options.
Phenylketonuria (PKU) Pipeline Trends and Insights
The year 2020 witnessed progress in innovations and the number of pipeline agents researched for Phenylketonuria (PKU) indication. The report presents near-term and long-term pipeline development trends and potential insights.
Phenylketonuria (PKU) Company Trends and Insights
The report analyzes the development progress, current status, investments, partnerships, and other developments of 15 companies. Business profiles and contact details of the companies actively perusing Phenylketonuria (PKU) pipeline are assessed.
Phenylketonuria (PKU) R&D Pipeline Development Phase Trends and Insights
From the discovery stage of development to phase 3 development, all the potential pipeline drug candidates are analyzed in the report. Phenylketonuria (PKU) discovery stage, research stage, Phase 1, phase 2, Phase 3, IND enabling studies are provided in the research.
Small Phenylketonuria (PKU) companies look for licensing and collaboration partners
High R&D costs and long duration pose challenges for small companies operating in the industry. Further, the presence of large companies and stringent regulations act as barriers for Phenylketonuria (PKU) pipeline development companies. Accordingly, a significant portion of small companies presents potential licensing and collaboration opportunities.
Phenylketonuria (PKU) Pipeline Market News and Developments during 2020
The Phenylketonuria (PKU) industry news, pipeline research, market developments including advancement in phases, pre-clinical study results, clinical trial launches, acquisitions and mergers, regulatory approvals, and others are included in the report.
Phenylketonuria (PKU) Mechanism of Action and Targets
Leading Mechanism of Action and targets being researched by all the companies and their progress is included. New mechanisms of actions introduced during the year, route of administration, orphan drug designation, and others are provided in the study.
New molecular entity details
Drug candidates identified as new molecular entities by FDA, EMA, and other regulators are included in the research.
Sources and Research Methodology
Data is updated daily across diseases in the infectious pipeline service. We review our quarterly pipeline reports for the latest 5 years to present longitudinal insights.
Scope and Coverage
- Phenylketonuria (PKU) pipeline development activities across the early phase, mid-stage, and late phase pipelines including therapeutic candidates
- Drug profiles comprising of drug overview, mechanism of action, co-developers, originators, route of administration, molecule type, orphan drug status, new molecular entity, area, and other details.
- Company-company partnerships, company-institute partnerships, and investment details of companies are included
- 15 companies are included including Agios Pharmaceuticals Inc, American Gene Technologies International In, APR Applied Pharma Research SA, BioMarin Pharmaceutical Inc, Codexis Inc, Generation Bio Corp, Homology Medicines Inc, MipSalus ApS, Moderna Therapeutics Inc, Nestle Health Science SA, Pluvia AS, PTC Therapeutics Inc, Sangamo Therapeutics Inc, SOM Biotech SL, Synlogic Inc,
- Disease overview, Pipeline trends, market analysis, and other developments
- Potential licensing/new business opportunities in Phenylketonuria (PKU) pipeline market
- Global coverage of companies and pipeline agents
- 2020 Trends, market analysis, and developments
- Potential growth opportunities
- Comprehensive details of drug candidates
- Drive pipeline research and commercial assessment
- Assess most promising drug candidates and stay ahead of the competition
- Strengthen your pipeline through identifying business expansion and acquisition opportunities
- Develop new candidates based on most focused targets and mechanism of actions
1. TABLE OF CONTENTS
1.1 List of Tables
1.2 List of Figures
2. PHENYLKETONURIA (PKU) PIPELINE TRENDS AND INSIGHTS
2.1 Dominant Phase type of Phenylketonuria (PKU) Pipeline, 2020
2.2 Most focused Mechanism of Action in Phenylketonuria (PKU) Pipeline
2.3 Leading type of Route of Administration during 2020
2.4 Proportion of New Molecular Entities in Phenylketonuria (PKU) pipeline
2.5 Active Companies Developing Phenylketonuria (PKU) pipeline
3. PHENYLKETONURIA (PKU) DISEASE TYPES, SYMPTOMS, CAUSES, AND AVAILABLE TREATMENT OPTIONS
3.1 Disease Overview
3.2 Types
3.3 Symptoms
3.4 Approved Treatment Options
4. PHENYLKETONURIA (PKU) PIPELINE COMPANY TRENDS AND INSIGHTS - BUSINESS PROFILES, DRUG CANDIDATES AND CONTACTS
4.1 Agios Pharmaceuticals Inc
American Gene Technologies International In
APR Applied Pharma Research SA
BioMarin Pharmaceutical Inc
Codexis Inc
Generation Bio Corp
Homology Medicines Inc
MipSalus ApS
Moderna Therapeutics Inc
Nestle Health Science SA
Pluvia AS
PTC Therapeutics Inc
Sangamo Therapeutics Inc
SOM Biotech SL
Synlogic Inc
5. PHENYLKETONURIA (PKU) PIPELINE DRUG PROFILES
5.1 Current Status of Drug and Vaccine Candidates
5.2 Drug Snapshot
5.2.1 Drug
5.2.2 Mechanism of Action
5.2.3 Phase
5.2.4 Co-Developer
5.2.5 Originator
5.2.6 Synonym
5.2.7 Route of Administration
5.2.8 Type of Molecule
5.2.9 Orphan Drug Status
5.2.10 New Molecular Entity
5.2.11 Area
5.3 Drug Details
5.4 Mechanism of Action
5.5 Licensing/Collaboration Agreements
5.6 Clinical Trial Details
6. PHENYLKETONURIA (PKU) PIPELINE MARKET NEWS AND DEVELOPMENTS DURING 2020
7. APPENDIX
7.1 About the Publisher
7.2 Sources and Research Methodology
1.1 List of Tables
1.2 List of Figures
2. PHENYLKETONURIA (PKU) PIPELINE TRENDS AND INSIGHTS
2.1 Dominant Phase type of Phenylketonuria (PKU) Pipeline, 2020
2.2 Most focused Mechanism of Action in Phenylketonuria (PKU) Pipeline
2.3 Leading type of Route of Administration during 2020
2.4 Proportion of New Molecular Entities in Phenylketonuria (PKU) pipeline
2.5 Active Companies Developing Phenylketonuria (PKU) pipeline
3. PHENYLKETONURIA (PKU) DISEASE TYPES, SYMPTOMS, CAUSES, AND AVAILABLE TREATMENT OPTIONS
3.1 Disease Overview
3.2 Types
3.3 Symptoms
3.4 Approved Treatment Options
4. PHENYLKETONURIA (PKU) PIPELINE COMPANY TRENDS AND INSIGHTS - BUSINESS PROFILES, DRUG CANDIDATES AND CONTACTS
4.1 Agios Pharmaceuticals Inc
American Gene Technologies International In
APR Applied Pharma Research SA
BioMarin Pharmaceutical Inc
Codexis Inc
Generation Bio Corp
Homology Medicines Inc
MipSalus ApS
Moderna Therapeutics Inc
Nestle Health Science SA
Pluvia AS
PTC Therapeutics Inc
Sangamo Therapeutics Inc
SOM Biotech SL
Synlogic Inc
5. PHENYLKETONURIA (PKU) PIPELINE DRUG PROFILES
5.1 Current Status of Drug and Vaccine Candidates
5.2 Drug Snapshot
5.2.1 Drug
5.2.2 Mechanism of Action
5.2.3 Phase
5.2.4 Co-Developer
5.2.5 Originator
5.2.6 Synonym
5.2.7 Route of Administration
5.2.8 Type of Molecule
5.2.9 Orphan Drug Status
5.2.10 New Molecular Entity
5.2.11 Area
5.3 Drug Details
5.4 Mechanism of Action
5.5 Licensing/Collaboration Agreements
5.6 Clinical Trial Details
6. PHENYLKETONURIA (PKU) PIPELINE MARKET NEWS AND DEVELOPMENTS DURING 2020
7. APPENDIX
7.1 About the Publisher
7.2 Sources and Research Methodology
