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Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Growth (Status and Outlook) 2023-2029

March 2023 | 101 pages | ID: G8CB62382FF0EN
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AAV is transformed from a naturally occurring virus into a delivery mechanism for gene therapy. The viral DNA is replaced with new DNA, and it becomes a precisely coded vector and is no longer considered a virus, as most of the viral components have been replaced. The AAV Vector-Based Gene Therapy market size is anticipated to shoot up exponentially attributing to an increase in the approval of a growing number of gene therapies and readily adoption on approval, ability to treat a broad array of conditions, increasing prevalence of diseases, convenient one-time dosing approach and curative treatment options.

LPI (LP Information)' newest research report, the “Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Industry Forecast” looks at past sales and reviews total world Adeno-Associated Virus (AAV) Vector-Based Gene Therapy sales in 2022, providing a comprehensive analysis by region and market sector of projected Adeno-Associated Virus (AAV) Vector-Based Gene Therapy sales for 2023 through 2029. With Adeno-Associated Virus (AAV) Vector-Based Gene Therapy sales broken down by region, market sector and sub-sector, this report provides a detailed analysis in US$ millions of the world Adeno-Associated Virus (AAV) Vector-Based Gene Therapy industry.

This Insight Report provides a comprehensive analysis of the global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy landscape and highlights key trends related to product segmentation, company formation, revenue, and market share, latest development, and M&A activity. This report also analyzes the strategies of leading global companies with a focus on Adeno-Associated Virus (AAV) Vector-Based Gene Therapy portfolios and capabilities, market entry strategies, market positions, and geographic footprints, to better understand these firms’ unique position in an accelerating global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy market.

This Insight Report evaluates the key market trends, drivers, and affecting factors shaping the global outlook for Adeno-Associated Virus (AAV) Vector-Based Gene Therapy and breaks down the forecast by type, by application, geography, and market size to highlight emerging pockets of opportunity. With a transparent methodology based on hundreds of bottom-up qualitative and quantitative market inputs, this study forecast offers a highly nuanced view of the current state and future trajectory in the global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy.

The global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy market size is projected to grow from US$ million in 2022 to US$ million in 2029; it is expected to grow at a CAGR of % from 2023 to 2029.

United States market for Adeno-Associated Virus (AAV) Vector-Based Gene Therapy is estimated to increase from US$ million in 2022 to US$ million by 2029, at a CAGR of % from 2023 through 2029.

China market for Adeno-Associated Virus (AAV) Vector-Based Gene Therapy is estimated to increase from US$ million in 2022 to US$ million by 2029, at a CAGR of % from 2023 through 2029.

Europe market for Adeno-Associated Virus (AAV) Vector-Based Gene Therapy is estimated to increase from US$ million in 2022 to US$ million by 2029, at a CAGR of % from 2023 through 2029.

Global key Adeno-Associated Virus (AAV) Vector-Based Gene Therapy players cover BioMarin Pharmaceutical, Sangamo Therapeutics, Amicus Therapeutics, Roche, Pfizer, NightstaRx, MeiraGTx, Sarepta Therapeutics and Neurocrine Biosciences, etc. In terms of revenue, the global two largest companies occupied for a share nearly % in 2022.

This report presents a comprehensive overview, market shares, and growth opportunities of Adeno-Associated Virus (AAV) Vector-Based Gene Therapy market by product type, application, key players and key regions and countries.

Market Segmentation:

Segmentation by type
  • Single-stranded AAV (ssAAV)
  • Self-complementary AAV (scAAV)
Segmentation by application
  • Hemophilia
  • Ophthalmology
  • Lysosomal Storage Disorders
  • Neurological Disorders
  • Others
This report also splits the market by region:
  • Americas
    • United States
    • Canada
    • Mexico
    • Brazil
  • APAC
    • China
    • Japan
    • Korea
    • Southeast Asia
    • India
    • Australia
  • Europe
    • Germany
    • France
    • UK
    • Italy
    • Russia
  • Middle East & Africa
    • Egypt
    • South Africa
    • Israel
    • Turkey
    • GCC Countries
The below companies that are profiled have been selected based on inputs gathered from primary experts and analyzing the company's coverage, product portfolio, its market penetration.
  • BioMarin Pharmaceutical
  • Sangamo Therapeutics
  • Amicus Therapeutics
  • Roche
  • Pfizer
  • NightstaRx
  • MeiraGTx
  • Sarepta Therapeutics
  • Neurocrine Biosciences
  • Voyager Therapeutics
  • Asklepios Biopharmaceutical
1 SCOPE OF THE REPORT

1.1 Market Introduction
1.2 Years Considered
1.3 Research Objectives
1.4 Market Research Methodology
1.5 Research Process and Data Source
1.6 Economic Indicators
1.7 Currency Considered
1.8 Market Estimation Caveats

2 EXECUTIVE SUMMARY

2.1 World Market Overview
  2.1.1 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2018-2029
  2.1.2 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size CAGR by Region 2018 VS 2022 VS 2029
2.2 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Segment by Type
  2.2.1 Single-stranded AAV (ssAAV)
  2.2.2 Self-complementary AAV (scAAV)
2.3 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type
  2.3.1 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size CAGR by Type (2018 VS 2022 VS 2029)
  2.3.2 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
2.4 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Segment by Application
  2.4.1 Hemophilia
  2.4.2 Ophthalmology
  2.4.3 Lysosomal Storage Disorders
  2.4.4 Neurological Disorders
  2.4.5 Others
2.5 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application
  2.5.1 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size CAGR by Application (2018 VS 2022 VS 2029)
  2.5.2 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)

3 ADENO-ASSOCIATED VIRUS (AAV) VECTOR-BASED GENE THERAPY MARKET SIZE BY PLAYER

3.1 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Players
  3.1.1 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue by Players (2018-2023)
  3.1.2 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Players (2018-2023)
3.2 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Key Players Head office and Products Offered
3.3 Market Concentration Rate Analysis
  3.3.1 Competition Landscape Analysis
  3.3.2 Concentration Ratio (CR3, CR5 and CR10) & (2021-2023)
3.4 New Products and Potential Entrants
3.5 Mergers & Acquisitions, Expansion

4 ADENO-ASSOCIATED VIRUS (AAV) VECTOR-BASED GENE THERAPY BY REGIONS

4.1 Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Regions (2018-2023)
4.2 Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth (2018-2023)
4.3 APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth (2018-2023)
4.4 Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth (2018-2023)
4.5 Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth (2018-2023)

5 AMERICAS

5.1 Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2018-2023)
5.2 Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023)
5.3 Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023)
5.4 United States
5.5 Canada
5.6 Mexico
5.7 Brazil

6 APAC

6.1 APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Region (2018-2023)
6.2 APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023)
6.3 APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023)
6.4 China
6.5 Japan
6.6 Korea
6.7 Southeast Asia
6.8 India
6.9 Australia

7 EUROPE

7.1 Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy by Country (2018-2023)
7.2 Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023)
7.3 Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023)
7.4 Germany
7.5 France
7.6 UK
7.7 Italy
7.8 Russia

8 MIDDLE EAST & AFRICA

8.1 Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy by Region (2018-2023)
8.2 Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023)
8.3 Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023)
8.4 Egypt
8.5 South Africa
8.6 Israel
8.7 Turkey
8.8 GCC Countries

9 MARKET DRIVERS, CHALLENGES AND TRENDS

9.1 Market Drivers & Growth Opportunities
9.2 Market Challenges & Risks
9.3 Industry Trends

10 GLOBAL ADENO-ASSOCIATED VIRUS (AAV) VECTOR-BASED GENE THERAPY MARKET FORECAST

10.1 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Regions (2024-2029)
  10.1.1 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Regions (2024-2029)
  10.1.2 Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast
  10.1.3 APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast
  10.1.4 Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast
  10.1.5 Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast
10.2 Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Country (2024-2029)
  10.2.1 United States Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.2.2 Canada Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.2.3 Mexico Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.2.4 Brazil Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
10.3 APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Region (2024-2029)
  10.3.1 China Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.3.2 Japan Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.3.3 Korea Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.3.4 Southeast Asia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.3.5 India Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.3.6 Australia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
10.4 Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Country (2024-2029)
  10.4.1 Germany Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.4.2 France Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.4.3 UK Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.4.4 Italy Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.4.5 Russia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
10.5 Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Region (2024-2029)
  10.5.1 Egypt Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.5.2 South Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.5.3 Israel Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.5.4 Turkey Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
  10.5.5 GCC Countries Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Forecast
10.6 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Type (2024-2029)
10.7 Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecast by Application (2024-2029)

11 KEY PLAYERS ANALYSIS

11.1 BioMarin Pharmaceutical
  11.1.1 BioMarin Pharmaceutical Company Information
  11.1.2 BioMarin Pharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.1.3 BioMarin Pharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.1.4 BioMarin Pharmaceutical Main Business Overview
  11.1.5 BioMarin Pharmaceutical Latest Developments
11.2 Sangamo Therapeutics
  11.2.1 Sangamo Therapeutics Company Information
  11.2.2 Sangamo Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.2.3 Sangamo Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.2.4 Sangamo Therapeutics Main Business Overview
  11.2.5 Sangamo Therapeutics Latest Developments
11.3 Amicus Therapeutics
  11.3.1 Amicus Therapeutics Company Information
  11.3.2 Amicus Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.3.3 Amicus Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.3.4 Amicus Therapeutics Main Business Overview
  11.3.5 Amicus Therapeutics Latest Developments
11.4 Roche
  11.4.1 Roche Company Information
  11.4.2 Roche Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.4.3 Roche Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.4.4 Roche Main Business Overview
  11.4.5 Roche Latest Developments
11.5 Pfizer
  11.5.1 Pfizer Company Information
  11.5.2 Pfizer Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.5.3 Pfizer Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.5.4 Pfizer Main Business Overview
  11.5.5 Pfizer Latest Developments
11.6 NightstaRx
  11.6.1 NightstaRx Company Information
  11.6.2 NightstaRx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.6.3 NightstaRx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.6.4 NightstaRx Main Business Overview
  11.6.5 NightstaRx Latest Developments
11.7 MeiraGTx
  11.7.1 MeiraGTx Company Information
  11.7.2 MeiraGTx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.7.3 MeiraGTx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.7.4 MeiraGTx Main Business Overview
  11.7.5 MeiraGTx Latest Developments
11.8 Sarepta Therapeutics
  11.8.1 Sarepta Therapeutics Company Information
  11.8.2 Sarepta Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.8.3 Sarepta Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.8.4 Sarepta Therapeutics Main Business Overview
  11.8.5 Sarepta Therapeutics Latest Developments
11.9 Neurocrine Biosciences
  11.9.1 Neurocrine Biosciences Company Information
  11.9.2 Neurocrine Biosciences Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.9.3 Neurocrine Biosciences Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.9.4 Neurocrine Biosciences Main Business Overview
  11.9.5 Neurocrine Biosciences Latest Developments
11.10 Voyager Therapeutics
  11.10.1 Voyager Therapeutics Company Information
  11.10.2 Voyager Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.10.3 Voyager Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.10.4 Voyager Therapeutics Main Business Overview
  11.10.5 Voyager Therapeutics Latest Developments
11.11 Asklepios Biopharmaceutical
  11.11.1 Asklepios Biopharmaceutical Company Information
  11.11.2 Asklepios Biopharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
  11.11.3 Asklepios Biopharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue, Gross Margin and Market Share (2018-2023)
  11.11.4 Asklepios Biopharmaceutical Main Business Overview
  11.11.5 Asklepios Biopharmaceutical Latest Developments

12 RESEARCH FINDINGS AND CONCLUSION
LIST OF TABLES

Table 1. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size CAGR by Region (2018 VS 2022 VS 2029) & ($ Millions)
Table 2. Major Players of Single-stranded AAV (ssAAV)
Table 3. Major Players of Self-complementary AAV (scAAV)
Table 4. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size CAGR by Type (2018 VS 2022 VS 2029) & ($ Millions)
Table 5. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023) & ($ Millions)
Table 6. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
Table 7. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size CAGR by Application (2018 VS 2022 VS 2029) & ($ Millions)
Table 8. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023) & ($ Millions)
Table 9. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)
Table 10. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue by Players (2018-2023) & ($ Millions)
Table 11. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Player (2018-2023)
Table 12. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Key Players Head office and Products Offered
Table 13. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Concentration Ratio (CR3, CR5 and CR10) & (2021-2023)
Table 14. New Products and Potential Entrants
Table 15. Mergers & Acquisitions, Expansion
Table 16. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Regions 2018-2023 & ($ Millions)
Table 17. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Regions (2018-2023)
Table 18. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue by Country/Region (2018-2023) & ($ millions)
Table 19. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Country/Region (2018-2023)
Table 20. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2018-2023) & ($ Millions)
Table 21. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Country (2018-2023)
Table 22. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023) & ($ Millions)
Table 23. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
Table 24. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023) & ($ Millions)
Table 25. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)
Table 26. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Region (2018-2023) & ($ Millions)
Table 27. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Region (2018-2023)
Table 28. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023) & ($ Millions)
Table 29. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
Table 30. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023) & ($ Millions)
Table 31. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)
Table 32. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2018-2023) & ($ Millions)
Table 33. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Country (2018-2023)
Table 34. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023) & ($ Millions)
Table 35. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
Table 36. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023) & ($ Millions)
Table 37. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)
Table 38. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Region (2018-2023) & ($ Millions)
Table 39. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Region (2018-2023)
Table 40. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2018-2023) & ($ Millions)
Table 41. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
Table 42. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2018-2023) & ($ Millions)
Table 43. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)
Table 44. Key Market Drivers & Growth Opportunities of Adeno-Associated Virus (AAV) Vector-Based Gene Therapy
Table 45. Key Market Challenges & Risks of Adeno-Associated Virus (AAV) Vector-Based Gene Therapy
Table 46. Key Industry Trends of Adeno-Associated Virus (AAV) Vector-Based Gene Therapy
Table 47. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Forecast by Regions (2024-2029) & ($ Millions)
Table 48. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share Forecast by Regions (2024-2029)
Table 49. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Forecast by Type (2024-2029) & ($ Millions)
Table 50. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Forecast by Application (2024-2029) & ($ Millions)
Table 51. BioMarin Pharmaceutical Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 52. BioMarin Pharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 53. BioMarin Pharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 54. BioMarin Pharmaceutical Main Business
Table 55. BioMarin Pharmaceutical Latest Developments
Table 56. Sangamo Therapeutics Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 57. Sangamo Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 58. Sangamo Therapeutics Main Business
Table 59. Sangamo Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 60. Sangamo Therapeutics Latest Developments
Table 61. Amicus Therapeutics Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 62. Amicus Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 63. Amicus Therapeutics Main Business
Table 64. Amicus Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 65. Amicus Therapeutics Latest Developments
Table 66. Roche Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 67. Roche Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 68. Roche Main Business
Table 69. Roche Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 70. Roche Latest Developments
Table 71. Pfizer Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 72. Pfizer Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 73. Pfizer Main Business
Table 74. Pfizer Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 75. Pfizer Latest Developments
Table 76. NightstaRx Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 77. NightstaRx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 78. NightstaRx Main Business
Table 79. NightstaRx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 80. NightstaRx Latest Developments
Table 81. MeiraGTx Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 82. MeiraGTx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 83. MeiraGTx Main Business
Table 84. MeiraGTx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 85. MeiraGTx Latest Developments
Table 86. Sarepta Therapeutics Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 87. Sarepta Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 88. Sarepta Therapeutics Main Business
Table 89. Sarepta Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 90. Sarepta Therapeutics Latest Developments
Table 91. Neurocrine Biosciences Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 92. Neurocrine Biosciences Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 93. Neurocrine Biosciences Main Business
Table 94. Neurocrine Biosciences Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 95. Neurocrine Biosciences Latest Developments
Table 96. Voyager Therapeutics Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 97. Voyager Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 98. Voyager Therapeutics Main Business
Table 99. Voyager Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 100. Voyager Therapeutics Latest Developments
Table 101. Asklepios Biopharmaceutical Details, Company Type, Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Area Served and Its Competitors
Table 102. Asklepios Biopharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product Offered
Table 103. Asklepios Biopharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue ($ million), Gross Margin and Market Share (2018-2023)
Table 104. Asklepios Biopharmaceutical Main Business
Table 105. Asklepios Biopharmaceutical Latest Developments

LIST OF FIGURES

Figure 1. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Report Years Considered
Figure 2. Research Objectives
Figure 3. Research Methodology
Figure 4. Research Process and Data Source
Figure 5. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth Rate 2018-2029 ($ Millions)
Figure 6. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Sales by Geographic Region (2018, 2022 & 2029) & ($ millions)
Figure 7. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Sales Market Share by Country/Region (2022)
Figure 8. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Sales Market Share by Country/Region (2018, 2022 & 2029)
Figure 9. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type in 2022
Figure 10. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy in Hemophilia
Figure 11. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market: Hemophilia (2018-2023) & ($ Millions)
Figure 12. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy in Ophthalmology
Figure 13. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market: Ophthalmology (2018-2023) & ($ Millions)
Figure 14. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy in Lysosomal Storage Disorders
Figure 15. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market: Lysosomal Storage Disorders (2018-2023) & ($ Millions)
Figure 16. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy in Neurological Disorders
Figure 17. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market: Neurological Disorders (2018-2023) & ($ Millions)
Figure 18. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy in Others
Figure 19. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market: Others (2018-2023) & ($ Millions)
Figure 20. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application in 2022
Figure 21. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Player in 2022
Figure 22. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Regions (2018-2023)
Figure 23. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2018-2023 ($ Millions)
Figure 24. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2018-2023 ($ Millions)
Figure 25. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2018-2023 ($ Millions)
Figure 26. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2018-2023 ($ Millions)
Figure 27. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Value Market Share by Country in 2022
Figure 28. United States Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 29. Canada Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 30. Mexico Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 31. Brazil Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 32. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Region in 2022
Figure 33. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type in 2022
Figure 34. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application in 2022
Figure 35. China Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 36. Japan Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 37. Korea Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 38. Southeast Asia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 39. India Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 40. Australia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 41. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Country in 2022
Figure 42. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
Figure 43. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)
Figure 44. Germany Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 45. France Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 46. UK Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 47. Italy Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 48. Russia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 49. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Region (2018-2023)
Figure 50. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Type (2018-2023)
Figure 51. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share by Application (2018-2023)
Figure 52. Egypt Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 53. South Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 54. Israel Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 55. Turkey Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 56. GCC Country Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth 2018-2023 ($ Millions)
Figure 57. Americas Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 58. APAC Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 59. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 60. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 61. United States Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 62. Canada Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 63. Mexico Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 64. Brazil Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 65. China Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 66. Japan Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 67. Korea Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 68. Southeast Asia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 69. India Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 70. Australia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 71. Germany Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 72. France Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 73. UK Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 74. Italy Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 75. Russia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 76. Spain Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 77. Egypt Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 78. South Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 79. Israel Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 80. Turkey Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 81. GCC Countries Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size 2024-2029 ($ Millions)
Figure 82. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share Forecast by Type (2024-2029)
Figure 83. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Market Share Forecast by Application (2024-2029)


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