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Orphan Drugs Market Size, Trends, Analysis, and Outlook By Drug (Biological, Non-biological), By Disease (Oncology, Hematology, Neurology, Cardiovascular, Others), By Distribution Channel (Hospital, Pharmacy, Online sales, Others), by Region, Country, Segment, and Companies, 2024-2030

March 2024 | 190 pages | ID: OD279126BCF1EN
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The global Orphan Drugs market size is poised to register 13.55% growth from 2024 to 2030, presenting significant growth prospects for companies operating in the industry. The industry study analyzes the global Orphan Drugs market across By Drug (Biological, Non-biological), By Disease (Oncology, Hematology, Neurology, Cardiovascular, Others), By Distribution Channel (Hospital, Pharmacy, Online sales, Others).

The Orphan Drugs market continues to expand rapidly, driven by regulatory incentives, increasing investment in rare disease research, advancements in biotechnology, and growing collaborations between pharmaceutical companies and research institutions. Orphan drugs are medications developed to treat rare diseases or conditions that affect a small number of patients, often characterized by high unmet medical needs, limited treatment options, and significant morbidity and mortality. Key factors fueling market growth include the rising prevalence of rare diseases, expanding orphan drug designations and approvals by regulatory agencies, and favorable government policies and incentives to encourage orphan drug development, such as orphan drug designation, market exclusivity, and tax credits. Additionally, the growing understanding of rare disease biology and genetics, coupled with advancements in precision medicine and genomic technologies, are accelerating drug discovery and development in the orphan drug space. Moreover, the increasing focus of pharmaceutical companies on rare diseases as a lucrative market opportunity, along with the emergence of patient advocacy groups and rare disease communities advocating for better access to treatments, is driving innovation and investment in the orphan drugs market. Furthermore, the expanding orphan drug pipelines, growing adoption of biologics and gene therapies, and rising healthcare expenditure on rare disease management are expected to sustain market growth. With the continued emphasis on addressing unmet medical needs in rare diseases and improving patient access to innovative therapies, the orphan drugs market is poised for further expansion and significant contributions to global healthcare.

Orphan Drugs Market Drivers, Trends, Opportunities, and Growth Opportunities

This comprehensive study discusses the latest trends and the most pressing challenges for industry players and investors. The Orphan Drugs market research analyses the global market trends, key drivers, challenges, and opportunities in the industry. In addition, the latest Future of Orphan Drugs survey report provides the market size outlook across types, applications, and other segments across the world and regions. It provides data-driven insights and actionable recommendations for companies in the Orphan Drugs industry.

Key market trends defining the global Orphan Drugs demand in 2024 and Beyond

The industry continues to remain an attractive hub for opportunities for both domestic and global vendors. As the market evolves, factors such as emerging market dynamics, demand from end-user sectors, a growing patient base, changes in consumption patterns, and widening distribution channels continue to play a major role.

Orphan Drugs Market Segmentation- Industry Share, Market Size, and Outlook to 2030

The Orphan Drugs industry comprises a wide range of segments and sub-segments. The rising demand for these product types and applications is supporting companies to increase their investment levels across niche segments. Accordingly, leading companies plan to generate a large share of their future revenue growth from expansion into these niche segments. The report presents the market size outlook across segments to support Orphan Drugs companies scaling up production in these sub-segments with a focus on expanding into emerging countries.

Key strategies adopted by companies within the Orphan Drugs industry

Leading Orphan Drugs companies are boosting investments to capitalize on untapped potential and future possibilities across niche market segments and surging demand conditions in key regions. Further, companies are leveraging advanced technologies to unlock opportunities and achieve operational excellence. The report provides key strategies opted for by the top 10 Orphan Drugs companies.

Orphan Drugs Market Study- Strategic Analysis Review

The Orphan Drugs market research report dives deep into the qualitative factors shaping the market, empowering you to make informed decisions-
  • Industry Dynamics: Porter's Five Forces analysis to understand bargaining power, competitive rivalry, and threats that impact long-term strategy formulation.
  • Strategic Insights: Provides valuable perspectives on key players and their approaches based on comprehensive strategy analysis.
  • Internal Strengths and Weaknesses: Develop targeted strategies to leverage strengths, address weaknesses, and capitalize on market opportunities.
  • Future Possibilities: Prepare for diverse outcomes with in-depth scenario analysis. Explore potential market disruptions, technology advancements, and economic changes.
Orphan Drugs Market Size Outlook- Historic and Forecast Revenue in Three Cases

The Orphan Drugs industry report provides a detailed analysis and outlook of revenue generated by companies from 2018 to 2023. Further, with actual data for 2023, the report forecasts the market size outlook from 2024 to 2030 in three case scenarios- low case, reference case, and high case scenarios.

Orphan Drugs Country Analysis and Revenue Outlook to 2030

The report analyses 22 countries worldwide including the key driving forces and market size outlook from 2021 to 2030. In addition, region analysis across Asia Pacific, Europe, the Middle East, Africa, North America, and South America is included in the study. For each of the six regions, the market size outlook by segments is forecast for 2030.

North America Orphan Drugs Market Size Outlook- Companies plan for focused investments in a changing environment

The US continues to remain the market leader in North America, driven by a large consumer base, the presence of well-established providers, and a strong end-user industry demand. Leading companies focus on new product launches in the changing environment. The US economy is expected to grow in 2024 (around 2.2% growth in 2024), potentially driving demand for various Orphan Drugs market segments. Similarly, Strong end-user demand is encouraging Canadian Orphan Drugs companies to invest in niche segments. Further, as Mexico continues to strengthen its trade relations and invest in technological advancements, the Mexico Orphan Drugs market is expected to experience significant expansion, offering lucrative opportunities for both domestic and international stakeholders.

Europe Orphan Drugs Market Size Outlook-Companies investing in assessing consumers, categories, competitors, and capabilities

The German industry remains the major market for companies in the European Orphan Drugs industry with consumers in Germany, France, the UK, Spain, Italy, and others anticipated to register a steady demand throughout the forecast period, driving the overall market prospects. In addition, the proactive approach of businesses in identifying and leveraging new growth prospects positions the European Orphan Drugs market for an upward trajectory, fostering both domestic and international interest. Leading brands operating in the industry are emphasizing effective marketing strategies, innovative product offerings, and a keen understanding of consumer preferences.

Asia Pacific Orphan Drugs Market Size Outlook- an attractive hub for opportunities for both local and global companies

The increasing prevalence of indications, robust healthcare expenditure, and increasing investments in healthcare infrastructure drive the demand for Orphan Drugs in Asia Pacific. In particular, China, India, and South East Asian Orphan Drugs markets present a compelling outlook for 2030, acting as a magnet for both domestic and multinational manufacturers seeking growth opportunities. Similarly, with a burgeoning population and a rising middle class, India offers a vast consumer market. Japanese and Korean companies are quickly aligning their strategies to navigate changes, explore new markets, and enhance their competitive edge. Our report utilizes in-depth interviews with industry experts and comprehensive data analysis to provide a comprehensive outlook of 6 major markets in the region.

Latin America Orphan Drugs Market Size Outlook- Continued urbanization and rising income levels

Rising income levels contribute to greater purchasing power among consumers, spurring consumption and creating opportunities for market expansion. Continued urbanization and rising income levels are expected to sustainably drive consumption growth in the medium to long term.

Middle East and Africa Orphan Drugs Market Size Outlook- continues its upward trajectory across segments

Robust demand from Middle Eastern countries including Saudi Arabia, the UAE, Qatar, Kuwait, and other GCC countries supports the overall Middle East Orphan Drugs market potential. Fueled by increasing healthcare expenditure of individuals, growing population, and high prevalence across a few markets drives the demand for Orphan Drugs.

Orphan Drugs Market Company Profiles

The global Orphan Drugs market is characterized by intense competitive conditions with leading companies opting for aggressive marketing to gain market shares. The report presents business descriptions, SWOT analysis, growth strategies, and financial profiles. Leading companies included in the study are AbbVie Inc, Alexion Pharmaceuticals Inc, Bristol-Myers Squibb Company, F. Hoffmann-La Roche Ltd, GSK plc, Johnson & Johnson Private Ltd, Merck & Co. Inc, Novartis AG, Pfizer Inc, Sanofi

Recent Orphan Drugs Market Developments

The global Orphan Drugs market study presents recent market news and developments including new product launches, mergers, acquisitions, expansions, product approvals, and other updates in the industry.

Orphan Drugs Market Report Scope

Parameters: Revenue, Volume Price

Study Period: 2023 (Base Year); 2018- 2023 (Historic Period); 2024- 2030 (Forecast Period)

Currency: USD; (Upon request, can be provided in Euro, JPY, GBP, and other Local Currency)

Qualitative Analysis
  • Pricing Analysis
  • Value Chain Analysis
  • SWOT Profile
  • Market Dynamics- Trends, Drivers, Challenges
  • Porter’s Five Forces Analysis
  • Macroeconomic Impact Analysis
  • Case Scenarios- Low, Base, High
Market Segmentation:

By Drug

Biological

Non-biological

By Disease

Oncology

Hematology

Neurology

Cardiovascular

Others

By Distribution Channel

Hospital

Pharmacy

Online sales

Others

Geographical Segmentation:
  • North America (3 markets)
  • Europe (6 markets)
  • Asia Pacific (6 markets)
  • Latin America (3 markets)
  • Middle East Africa (5 markets)
Companies

AbbVie Inc

Alexion Pharmaceuticals Inc

Bristol-Myers Squibb Company

F. Hoffmann-La Roche Ltd

GSK plc

Johnson & Johnson Private Ltd

Merck & Co. Inc

Novartis AG

Pfizer Inc

Sanofi

Formats Available: Excel, PDF, and PPT
1. EXECUTIVE SUMMARY

1.1 Orphan Drugs Market Overview and Key Findings, 2024
1.2 Orphan Drugs Market Size and Growth Outlook, 2021- 2030
1.3 Orphan Drugs Market Growth Opportunities to 2030
1.4 Key Orphan Drugs Market Trends and Challenges
  1.4.1 Orphan Drugs Market Drivers and Trends
  1.4.2 Orphan Drugs Market Challenges
1.5 Competitive Landscape and Key Players
1.6 Competitive Analysis- Growth Strategies Adopted by Leading Orphan Drugs Companies

2. ORPHAN DRUGS MARKET SIZE OUTLOOK TO 2030

2.1 Orphan Drugs Market Size Outlook, USD Million, 2021- 2030
2.2 Orphan Drugs Incremental Market Growth Outlook, %, 2021- 2030
2.3 Segment Snapshot, 2024

3. ORPHAN DRUGS MARKET- STRATEGIC ANALYSIS REVIEW

3.1 Porter's Five Forces Analysis
* Threat of New Entrants
* Threat of Substitutes
* Intensity of Competitive Rivalry
* Bargaining Power of Buyers
* Bargaining Power of Suppliers
3.2 Value Chain Analysis
3.3 SWOT Analysis

4. ORPHAN DRUGS MARKET SEGMENTATION ANALYSIS AND OUTLOOK

4.1 Market Segmentation and Scope
4.2 Market Breakdown by Type, Application, and Other Segments, 2021-2030
By Drug
Biological
Non-biological
By Disease
Oncology
Hematology
Neurology
Cardiovascular
Others
By Distribution Channel
Hospital
Pharmacy
Online sales
Others
4.3 Growth Prospects and Niche Opportunities, 2023- 2030
4.4 Regional comparison of Market Growth, CAGR, 2023-2030

5. REGION-WISE MARKET OUTLOOK TO 2030

5.1 Key Findings for Asia Pacific Orphan Drugs Market, 2025
5.2 Asia Pacific Orphan Drugs Market Size Outlook by Type, 2021- 2030
5.3 Asia Pacific Orphan Drugs Market Size Outlook by Application, 2021- 2030
5.4 Key Findings for Europe Orphan Drugs Market, 2025
5.5 Europe Orphan Drugs Market Size Outlook by Type, 2021- 2030
5.6 Europe Orphan Drugs Market Size Outlook by Application, 2021- 2030
5.7 Key Findings for North America Orphan Drugs Market, 2025
5.8 North America Orphan Drugs Market Size Outlook by Type, 2021- 2030
5.9 North America Orphan Drugs Market Size Outlook by Application, 2021- 2030
5.10 Key Findings for South America Orphan Drugs Market, 2025
5.11 South America Pacific Orphan Drugs Market Size Outlook by Type, 2021- 2030
5.12 South America Orphan Drugs Market Size Outlook by Application, 2021- 2030
5.13 Key Findings for Middle East and Africa Orphan Drugs Market, 2025
5.14 Middle East Africa Orphan Drugs Market Size Outlook by Type, 2021- 2030
5.15 Middle East Africa Orphan Drugs Market Size Outlook by Application, 2021- 2030

6. COUNTRY-WISE MARKET SIZE OUTLOOK TO 2030

6.1 US Orphan Drugs Market Size Outlook and Revenue Growth Forecasts
6.2 US Orphan Drugs Industry Drivers and Opportunities
6.3 Canada Market Size Outlook and Revenue Growth Forecasts
6.4 Canada Orphan Drugs Industry Drivers and Opportunities
6.6 Mexico Market Size Outlook and Revenue Growth Forecasts
6.6 Mexico Orphan Drugs Industry Drivers and Opportunities
6.7 Germany Market Size Outlook and Revenue Growth Forecasts
6.8 Germany Orphan Drugs Industry Drivers and Opportunities
6.9 France Market Size Outlook and Revenue Growth Forecasts
6.10 France Orphan Drugs Industry Drivers and Opportunities
6.11 UK Market Size Outlook and Revenue Growth Forecasts
6.12 UK Orphan Drugs Industry Drivers and Opportunities
6.13 Spain Market Size Outlook and Revenue Growth Forecasts
6.14 Spain Orphan Drugs Industry Drivers and Opportunities
6.16 Italy Market Size Outlook and Revenue Growth Forecasts
6.16 Italy Orphan Drugs Industry Drivers and Opportunities
6.17 Rest of Europe Market Size Outlook and Revenue Growth Forecasts
6.18 Rest of Europe Orphan Drugs Industry Drivers and Opportunities
6.19 China Market Size Outlook and Revenue Growth Forecasts
6.20 China Orphan Drugs Industry Drivers and Opportunities
6.21 India Market Size Outlook and Revenue Growth Forecasts
6.22 India Orphan Drugs Industry Drivers and Opportunities
6.23 Japan Market Size Outlook and Revenue Growth Forecasts
6.24 Japan Orphan Drugs Industry Drivers and Opportunities
6.26 South Korea Market Size Outlook and Revenue Growth Forecasts
6.26 South Korea Orphan Drugs Industry Drivers and Opportunities
6.27 Australia Market Size Outlook and Revenue Growth Forecasts
6.28 Australia Orphan Drugs Industry Drivers and Opportunities
6.29 South East Asia Market Size Outlook and Revenue Growth Forecasts
6.30 South East Asia Orphan Drugs Industry Drivers and Opportunities
6.31 Rest of Asia Pacific Market Size Outlook and Revenue Growth Forecasts
6.32 Rest of Asia Pacific Orphan Drugs Industry Drivers and Opportunities
6.33 Brazil Market Size Outlook and Revenue Growth Forecasts
6.34 Brazil Orphan Drugs Industry Drivers and Opportunities
6.36 Argentina Market Size Outlook and Revenue Growth Forecasts
6.36 Argentina Orphan Drugs Industry Drivers and Opportunities
6.37 Rest of South America Market Size Outlook and Revenue Growth Forecasts
6.38 Rest of South America Orphan Drugs Industry Drivers and Opportunities
6.39 Middle East Market Size Outlook and Revenue Growth Forecasts
6.40 Middle East Orphan Drugs Industry Drivers and Opportunities
6.41 Africa Market Size Outlook and Revenue Growth Forecasts
6.42 Africa Orphan Drugs Industry Drivers and Opportunities

7. ORPHAN DRUGS MARKET OUTLOOK ACROSS SCENARIOS

7.1 Low Growth Case
7.2 Reference Growth Case
7.3 High Growth Case

8. ORPHAN DRUGS COMPANY PROFILES

8.1 Profiles of Leading Orphan Drugs Companies in the Market
8.2 Business Descriptions, SWOT Analysis, and Growth Strategies
8.3 Financial Performance and Key Metrics
AbbVie Inc
Alexion Pharmaceuticals Inc
Bristol-Myers Squibb Company
F. Hoffmann-La Roche Ltd
GSK plc
Johnson & Johnson Private Ltd
Merck & Co. Inc
Novartis AG
Pfizer Inc
Sanofi

9. APPENDIX

9.1 Scope of the Report
9.2 Research Methodology and Data Sources
9.3 Glossary of Terms
9.4 Market Definitions
9.5 Contact Information


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