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2019 Future of Rett Syndrome R&D Pipeline Drugs and Companies- Analysis of Pipeline Compounds, Phases, Mechanism of Action, Clinical Trials and Developments

February 2019 | 80 pages | ID: 25EBD42D1E0EN
VPAResearch

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The global demand for Rett Syndrome treatment options is emerging rapidly driven by demand in major emerging and developed markets. An increasing number of companies are working on Rett Syndrome pipeline. Companies quickly adapting to the new technologies both independently and through collaborations and advancing their pipeline candidates to advanced phases will evolve as top performers. However, challenges of completing clinical trials on schedules and limited financial support are holding some of the Rett Syndrome pipeline companies from advancing their products into Phase 3 or Phase 4.

Rett Syndrome Report Description-

The 2019 pipeline study on Rett Syndrome pipeline is a comprehensive research on the drug candidates across different phases. This research study evaluates each of the pipeline products in terms of their current status, regulatory progress and expected phase completion date. Focusing on the factors driving and challenging pipeline drug development, this strategic analysis review presents detailed analysis on all active Rett Syndrome pipeline compounds.

The Rett Syndrome pipeline guide presents information on all active drugs currently being developed for Rett Syndrome. The research work provides details of active therapeutic candidates in different phases including discovery, research, pre-clinical, phase I, Phase II, Phase III and pre-registration phases.

Details of current status, R&D progress and latest developments for every Rett Syndrome pipeline candidate are analyzed.

Further, current phase of development, mechanism of drug action, special designations such as orphan drug status, fast track designation, grants awarded, etc are presented for all Rett Syndrome drug candidates.

Drug development companies, collaborators, originating companies, license providers and universities participating in the Rett Syndrome product pipeline are provided. Company overview, snapshot and developments are provided for all participating companies.

The report assists in identifying potential upcoming companies and drugs in Rett Syndrome pipeline market along with progress of each drug. It also enables users to formulate effective strategies to stay ahead of competition.

VPA Research has developed a robust methodology for assessing pharmaceutical drugs, market sizes and sound forecast tools. All our research reports are provided through intense and repetitive primary and secondary research methods. Further, these reports are validated with industry experts to ensure reliability in the current scenario. The report is presented in a user-friendly format and presents clear and actionable insights.

Scope of Rett Syndrome pipeline report includes-
  • An overview of Rett Syndrome disease including symptoms, causes, diagnosis and available treatment options is provided.
  • Snapshot of pipeline detailing number of active compounds, mergers and acquisitions, phase wise compounds, target areas, mechanism of action, trials etc
  • Phase wise count of Rett Syndrome pipeline
  • Company wise list of Rett Syndrome pipeline
  • Mechanism of Action wise Rett Syndrome pipeline
    • For each pipeline candidate, the following details are provided
    • Snapshot (Drug, Mechanism of Action, Phase, Co Developer, Originator, Synonym, Orphan Drug Status, New Molecular Entity, Area)
    • Current status of development
    • Drug overview
    • Mechanism of Action
    • Pre-clinical and Clinical Trials/Results
  • Company Overview and Recent Developments
REASONS TO BUY
  • The report is designed to help industry executives promote the success and continued growth of their organizations
  • Get clear understanding of the entire Rett Syndrome pipeline, with details on active projects
  • Stay ahead of the competition through comprehensive knowledge of Rett Syndrome pipeline progress
  • Get in detail information of each product with updated information on each project along with key milestones
  • Gain clear insights into companies participating in Rett Syndrome pipeline along with progress of each of the company’s products and information on associations/collaborations/licensing data
  • Get trial information for each pipeline product under development
  • Understand the pipeline structure in terms of mechanism of Action, phase and company
The report will be delivered in 2 working days.
1. TABLE OF CONTENTS

1.1 List of Tables
1.2 List of Figures

2. GLOBAL RETT SYNDROME PIPELINE OVERVIEW

2.1 Key Findings, 2019
2.2 Disease Overview
2.3 Research Methodology

3. EXECUTIVE SUMMARY

3.1 Rett Syndrome Drugs under active development, H1- 2019
3.2 Pipeline Drugs in Early Stage of Development
  3.2.1 Pre-clinical
  3.2.2 Discovery
  3.2.3 Phase
  3.2.4Phase
3.3 Pipeline Drugs in Advanced Stage of Development
  3.3.1 Phase
  3.3.2 Pre-registration
3.4 Companies involved in Rett Syndrome pipeline, H1- 2019
3.5 Mechanism of Action wise Rett Syndrome Pipeline Candidates

4 AMO PHARMA LTD RETT SYNDROME PIPELINE DETAILS

4.1 AMO Pharma Ltd Business Profile
4.2 AMO Pharma Ltd Rett Syndrome Drug Details
4.3 Drug Snapshot
  4.3.1 Originator
  4.3.2 Collaborator/Co-Developer
  4.3.3 Route of Administration
  4.3.4 Orphan Drug/Fast Track/Special Designation
  4.3.5 Geography
  4.3.6 Type of Molecular Entity
  4.3.7 Current Status
4.4 Drug Overview
4.5 Drug Mechanism of Action
4.6 Clinical/Pre-clinical Trial Details
4.7 Latest Drug Developments

5 AMORSA THERAPEUTICS INC RETT SYNDROME PIPELINE DETAILS

5.1 Amorsa Therapeutics Inc Business Profile
5.2 Amorsa Therapeutics Inc Rett Syndrome Drug Details
5.3 Drug Snapshot
  5.3.1 Originator
  5.3.2 Collaborator/Co-Developer
  5.3.3 Route of Administration
  5.3.4 Orphan Drug/Fast Track/Special Designation
  5.3.5 Geography
  5.3.6 Type of Molecular Entity
  5.3.7 Current Status
5.4 Drug Overview
5.5 Drug Mechanism of Action
5.6 Clinical/Pre-clinical Trial Details
5.7 Latest Drug Developments

6 ANAVEX LIFE SCIENCES CORP RETT SYNDROME PIPELINE DETAILS

6.1 Anavex Life Sciences Corp Business Profile
6.2 Anavex Life Sciences Corp Rett Syndrome Drug Details
6.3 Drug Snapshot
  6.3.1 Originator
  6.3.2 Collaborator/Co-Developer
  6.3.3 Route of Administration
  6.3.4 Orphan Drug/Fast Track/Special Designation
  6.3.5 Geography
  6.3.6 Type of Molecular Entity
  6.3.7 Current Status
6.4 Drug Overview
6.5 Drug Mechanism of Action
6.6 Clinical/Pre-clinical Trial Details
6.7 Latest Drug Developments

7 ARMAGEN INC RETT SYNDROME PIPELINE DETAILS

7.1 ArmaGen Inc Business Profile
7.2 ArmaGen Inc Rett Syndrome Drug Details
7.3 Drug Snapshot
  7.3.1 Originator
  7.3.2 Collaborator/Co-Developer
  7.3.3 Route of Administration
  7.3.4 Orphan Drug/Fast Track/Special Designation
  7.3.5 Geography
  7.3.6 Type of Molecular Entity
  7.3.7 Current Status
7.4 Drug Overview
7.5 Drug Mechanism of Action
7.6 Clinical/Pre-clinical Trial Details
7.7 Latest Drug Developments

8 AVEXIS INC RETT SYNDROME PIPELINE DETAILS

8.1 AveXis Inc Business Profile
8.2 AveXis Inc Rett Syndrome Drug Details
8.3 Drug Snapshot
  8.3.1 Originator
  8.3.2 Collaborator/Co-Developer
  8.3.3 Route of Administration
  8.3.4 Orphan Drug/Fast Track/Special Designation
  8.3.5 Geography
  8.3.6 Type of Molecular Entity
  8.3.7 Current Status
8.4 Drug Overview
8.5 Drug Mechanism of Action
8.6 Clinical/Pre-clinical Trial Details
8.7 Latest Drug Developments

9 BIOHAVEN PHARMACEUTICAL HOLDING COMPANY LTD RETT SYNDROME PIPELINE DETAILS

9.1 Biohaven Pharmaceutical Holding Company Ltd Business Profile
9.2 Biohaven Pharmaceutical Holding Company Ltd Rett Syndrome Drug Details
9.3 Drug Snapshot
  9.3.1 Originator
  9.3.2 Collaborator/Co-Developer
  9.3.3 Route of Administration
  9.3.4 Orphan Drug/Fast Track/Special Designation
  9.3.5 Geography
  9.3.6 Type of Molecular Entity
  9.3.7 Current Status
9.4 Drug Overview
9.5 Drug Mechanism of Action
9.6 Clinical/Pre-clinical Trial Details
9.7 Latest Drug Developments

10 COLD SPRING HARBOR LABORATORY RETT SYNDROME PIPELINE DETAILS

10.1 Cold Spring Harbor Laboratory Business Profile
10.2 Cold Spring Harbor Laboratory Rett Syndrome Drug Details
10.3 Drug Snapshot
  10.3.1 Originator
  10.3.2 Collaborator/Co-Developer
  10.3.3 Route of Administration
  10.3.4 Orphan Drug/Fast Track/Special Designation
  10.3.5 Geography
  10.3.6 Type of Molecular Entity
  10.3.7 Current Status
10.4 Drug Overview
10.5 Drug Mechanism of Action
10.6 Clinical/Pre-clinical Trial Details
10.7 Latest Drug Developments

11 ELOXX PHARMACEUTICALS INC RETT SYNDROME PIPELINE DETAILS

11.1 Eloxx Pharmaceuticals Inc Business Profile
11.2 Eloxx Pharmaceuticals Inc Rett Syndrome Drug Details
11.3 Drug Snapshot
  11.3.1 Originator
  11.3.2 Collaborator/Co-Developer
  11.3.3 Route of Administration
  11.3.4 Orphan Drug/Fast Track/Special Designation
  11.3.5 Geography
  11.3.6 Type of Molecular Entity
  11.3.7 Current Status
11.4 Drug Overview
11.5 Drug Mechanism of Action
11.6 Clinical/Pre-clinical Trial Details
11.7 Latest Drug Developments

12 GW PHARMACEUTICALS PLC RETT SYNDROME PIPELINE DETAILS

12.1 GW Pharmaceuticals Plc Business Profile
12.2 GW Pharmaceuticals Plc Rett Syndrome Drug Details
12.3 Drug Snapshot
  12.3.1 Originator
  12.3.2 Collaborator/Co-Developer
  12.3.3 Route of Administration
  12.3.4 Orphan Drug/Fast Track/Special Designation
  12.3.5 Geography
  12.3.6 Type of Molecular Entity
  12.3.7 Current Status
12.4 Drug Overview
12.5 Drug Mechanism of Action
12.6 Clinical/Pre-clinical Trial Details
12.7 Latest Drug Developments

13 MITOCHON PHARMACEUTICALS INC RETT SYNDROME PIPELINE DETAILS

13.1 Mitochon Pharmaceuticals Inc Business Profile
13.2 Mitochon Pharmaceuticals Inc Rett Syndrome Drug Details
13.3 Drug Snapshot
  13.3.1 Originator
  13.3.2 Collaborator/Co-Developer
  13.3.3 Route of Administration
  13.3.4 Orphan Drug/Fast Track/Special Designation
  13.3.5 Geography
  13.3.6 Type of Molecular Entity
  13.3.7 Current Status
13.4 Drug Overview
13.5 Drug Mechanism of Action
13.6 Clinical/Pre-clinical Trial Details
13.7 Latest Drug Developments

14 MITSUBISHI TANABE PHARMA CORP RETT SYNDROME PIPELINE DETAILS

14.1 Mitsubishi Tanabe Pharma Corp Business Profile
14.2 Mitsubishi Tanabe Pharma Corp Rett Syndrome Drug Details
14.3 Drug Snapshot
  14.3.1 Originator
  14.3.2 Collaborator/Co-Developer
  14.3.3 Route of Administration
  14.3.4 Orphan Drug/Fast Track/Special Designation
  14.3.5 Geography
  14.3.6 Type of Molecular Entity
  14.3.7 Current Status
14.4 Drug Overview
14.5 Drug Mechanism of Action
14.6 Clinical/Pre-clinical Trial Details
14.7 Latest Drug Developments

15 NEUREN PHARMACEUTICALS LTD RETT SYNDROME PIPELINE DETAILS

15.1 Neuren Pharmaceuticals Ltd Business Profile
15.2 Neuren Pharmaceuticals Ltd Rett Syndrome Drug Details
15.3 Drug Snapshot
  15.3.1 Originator
  15.3.2 Collaborator/Co-Developer
  15.3.3 Route of Administration
  15.3.4 Orphan Drug/Fast Track/Special Designation
  15.3.5 Geography
  15.3.6 Type of Molecular Entity
  15.3.7 Current Status
15.4 Drug Overview
15.5 Drug Mechanism of Action
15.6 Clinical/Pre-clinical Trial Details
15.7 Latest Drug Developments

16 NEUROLIXIS INC RETT SYNDROME PIPELINE DETAILS

16.1 Neurolixis Inc Business Profile
16.2 Neurolixis Inc Rett Syndrome Drug Details
16.3 Drug Snapshot
  16.3.1 Originator
  16.3.2 Collaborator/Co-Developer
  16.3.3 Route of Administration
  16.3.4 Orphan Drug/Fast Track/Special Designation
  16.3.5 Geography
  16.3.6 Type of Molecular Entity
  16.3.7 Current Status
16.4 Drug Overview
16.5 Drug Mechanism of Action
16.6 Clinical/Pre-clinical Trial Details
16.7 Latest Drug Developments

17 NEUROTROPE BIOSCIENCE INC RETT SYNDROME PIPELINE DETAILS

17.1 Neurotrope Bioscience Inc Business Profile
17.2 Neurotrope Bioscience Inc Rett Syndrome Drug Details
17.3 Drug Snapshot
  17.3.1 Originator
  17.3.2 Collaborator/Co-Developer
  17.3.3 Route of Administration
  17.3.4 Orphan Drug/Fast Track/Special Designation
  17.3.5 Geography
  17.3.6 Type of Molecular Entity
  17.3.7 Current Status
17.4 Drug Overview
17.5 Drug Mechanism of Action
17.6 Clinical/Pre-clinical Trial Details
17.7 Latest Drug Developments

18 NEWRON PHARMACEUTICALS SPA RETT SYNDROME PIPELINE DETAILS

18.1 Newron Pharmaceuticals SpA Business Profile
18.2 Newron Pharmaceuticals SpA Rett Syndrome Drug Details
18.3 Drug Snapshot
  18.3.1 Originator
  18.3.2 Collaborator/Co-Developer
  18.3.3 Route of Administration
  18.3.4 Orphan Drug/Fast Track/Special Designation
  18.3.5 Geography
  18.3.6 Type of Molecular Entity
  18.3.7 Current Status
18.4 Drug Overview
18.5 Drug Mechanism of Action
18.6 Clinical/Pre-clinical Trial Details
18.7 Latest Drug Developments

19 OPKO HEALTH INC RETT SYNDROME PIPELINE DETAILS

19.1 OPKO Health Inc Business Profile
19.2 OPKO Health Inc Rett Syndrome Drug Details
19.3 Drug Snapshot
  19.3.1 Originator
  19.3.2 Collaborator/Co-Developer
  19.3.3 Route of Administration
  19.3.4 Orphan Drug/Fast Track/Special Designation
  19.3.5 Geography
  19.3.6 Type of Molecular Entity
  19.3.7 Current Status
19.4 Drug Overview
19.5 Drug Mechanism of Action
19.6 Clinical/Pre-clinical Trial Details
19.7 Latest Drug Developments

20 ORPHERIS INC RETT SYNDROME PIPELINE DETAILS

20.1 Orpheris Inc Business Profile
20.2 Orpheris Inc Rett Syndrome Drug Details
20.3 Drug Snapshot
  20.3.1 Originator
  20.3.2 Collaborator/Co-Developer
  20.3.3 Route of Administration
  20.3.4 Orphan Drug/Fast Track/Special Designation
  20.3.5 Geography
  20.3.6 Type of Molecular Entity
  20.3.7 Current Status
20.4 Drug Overview
20.5 Drug Mechanism of Action
20.6 Clinical/Pre-clinical Trial Details
20.7 Latest Drug Developments

21 PHARMATROPHIX INC RETT SYNDROME PIPELINE DETAILS

21.1 PharmatrophiX Inc Business Profile
21.2 PharmatrophiX Inc Rett Syndrome Drug Details
21.3 Drug Snapshot
  21.3.1 Originator
  21.3.2 Collaborator/Co-Developer
  21.3.3 Route of Administration
  21.3.4 Orphan Drug/Fast Track/Special Designation
  21.3.5 Geography
  21.3.6 Type of Molecular Entity
  21.3.7 Current Status
21.4 Drug Overview
21.5 Drug Mechanism of Action
21.6 Clinical/Pre-clinical Trial Details
21.7 Latest Drug Developments

22 RELMADA THERAPEUTICS INC RETT SYNDROME PIPELINE DETAILS

22.1 Relmada Therapeutics Inc Business Profile
22.2 Relmada Therapeutics Inc Rett Syndrome Drug Details
22.3 Drug Snapshot
  22.3.1 Originator
  22.3.2 Collaborator/Co-Developer
  22.3.3 Route of Administration
  22.3.4 Orphan Drug/Fast Track/Special Designation
  22.3.5 Geography
  22.3.6 Type of Molecular Entity
  22.3.7 Current Status
22.4 Drug Overview
22.5 Drug Mechanism of Action
22.6 Clinical/Pre-clinical Trial Details
22.7 Latest Drug Developments

23 STARWISE THERAPEUTICS LLC RETT SYNDROME PIPELINE DETAILS

23.1 Starwise Therapeutics LLC Business Profile
23.2 Starwise Therapeutics LLC Rett Syndrome Drug Details
23.3 Drug Snapshot
  23.3.1 Originator
  23.3.2 Collaborator/Co-Developer
  23.3.3 Route of Administration
  23.3.4 Orphan Drug/Fast Track/Special Designation
  23.3.5 Geography
  23.3.6 Type of Molecular Entity
  23.3.7 Current Status
23.4 Drug Overview
23.5 Drug Mechanism of Action
23.6 Clinical/Pre-clinical Trial Details
23.7 Latest Drug Developments

24 ULTRAGENYX PHARMACEUTICAL INC RETT SYNDROME PIPELINE DETAILS

24.1 Ultragenyx Pharmaceutical Inc Business Profile
24.2 Ultragenyx Pharmaceutical Inc Rett Syndrome Drug Details
24.3 Drug Snapshot
  24.3.1 Originator
  24.3.2 Collaborator/Co-Developer
  24.3.3 Route of Administration
  24.3.4 Orphan Drug/Fast Track/Special Designation
  24.3.5 Geography
  24.3.6 Type of Molecular Entity
  24.3.7 Current Status
24.4 Drug Overview
24.5 Drug Mechanism of Action
24.6 Clinical/Pre-clinical Trial Details
24.7 Latest Drug Developments

25. LATEST RETT SYNDROME DRUG PIPELINE DEVELOPMENTS, 2019

26. APPENDIX

26.1 About Us
26.2 Sources and Methodology
26.3 Contact Information


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